Stem cell hope for Duchenne muscular dystrophy
Duchenne muscular dystrophy (DMD) is an inherited disease that affects about one in every 4,000 males born in the USA. It is caused by mutations in the DMD gene that lead to the protein dystrophin...
View ArticleProgress towards a cure for Duchenne Muscular Dystrophy
Duchenne muscular dystrophy (DMD) is a severe inherited muscular dystrophy that causes progressive muscle degeneration which eventually leads to loss of the ability to use muscles and death, and every...
View ArticlePromising clinical trial result for exon skipping in Duchenne Muscular Dystrophy
Last Monday the Muscular Dystrophy Campaign announced that the antisense oligonucleotide drug AVI-4658 had performed well in its second clinical trial in 19 boys with Duchenne Muscular Dystrophy (DMD)....
View ArticleResearch Roundup: gene therapy for inherited blindness, urea implicated as a...
Welcome to this week’s Research Roundup. These Friday posts aim to inform our readers about the many stories that relate to animal research each week. Do you have an animal research story we should...
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